Our mission

Discover, develop, and commercialize a new class of RNA therapies informed by human genetics and disease biology to improve the lives of patients with debilitating and life-threatening diseases.

Our vision

Create transformative genetic medicines for rare and highly prevalent diseases

Meet our team

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Ram Aiyar, Ph.D., MBA

Chief Executive Officer & President

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Loïc Vincent, Ph.D.

Chief Scientific Officer

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Todd Chappell, MBA

Chief Operating Officer

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Jeffrey M. Cerio, Pharm.D., J.D.

SVP, General Counsel

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Stephanie Engels

Chief People Officer

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Gaozhong Zhu, Ph.D.

SVP, CMC & Technical Operations

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Ram Aiyar, Ph.D., MBA

Chief Executive Officer & President

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Ali Behbahani, M.D.

Director

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Nessan Bermingham, Ph.D.

Co-Founder & Chairman

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Jean-François Formela, M.D.

Co-Founder & Director

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Katharine Knobil, M.D.

Director

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Rachel Meyers, Ph.D.

Director

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Timothy R. Pearson

Director